Washington University School of Medicine

Division of Biostatistics
Seminar Series Spring 2008

Study Design Strategies to Evaluate Pharmacogenetic Testing and www.WarfarinDosing.org

Brian F. Gage MD, MSc (HSR)
Department of Internal Medicine, Division of General Medical Sciences
Washington University School of Medicine

Friday, January 18, 2008, 12:30–1:30 pm

GEMS classroom, 3rd Floor in Shriner's Building
Coffee, tea, and cookies will be provided


Abstract

Warfarin sodium (Coumadin(tm) and others) is a common blood thinner used to treat or prevent thromboembolic events in patients at high risk for clotting. Polymorphisms of two known genes (CYP2C9 and VKORC1) contribute 30% to the variation in dose requirements by altering warfarin metabolism and sensitivity. In recognition of warfarin's pharmacology, the FDA changed its labeling to encourage, but not require pharmacogenetic testing when warfarin is initiated. To prevent bleeding due to overdose and thrombosis from under-dosing, we developed pharmacogenetic algorithms that incorporate genotype and traditional factors available when warfarin is initiated. Prospective, open-labeled use of the algorithms demonstrates greater accuracy than clinical dosing and suggests a 20% reduction in clinical adverse events. However, a multi-centered, randomized controlled trial of clinical and pharmacogenetic approaches has yet to be done.

In this talk we will discuss study design strategies for a multicentered, randomized trial of warfarin therapy. In particular, we will discuss: methods of double-blinding, a study website (www.WarfarinDosing.org), use of an intermediate outcome (INR control), enhancement of certain genotypes, and the efficiency of testing for an interaction between genotype and group.

This work is joint with Petra (Jacobsen) Lenzini, MSc (GEMS).